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FDA grants orphan drug status to potential treatment for ALL - Rare Cancer NewsRare Cancer News · Fri, 07 Aug 2026 18:08:50 GMTGalibra Neuroscience Receives FDA Orphan Drug and Rare Pediatric Disease Designations for SSADH Deficiency Gene Therapy - deltanews.tvdeltanews.tv · Thu, 06 Aug 2026 01:05:00 GMTThe latest orphan drug exemptions may not be warranted, analysis finds - STATSTAT · Tue, 04 Aug 2026 12:09:35 GMTU.S. FDA Grants Orphan Drug Designation to Zai Lab’s DLL3-Targeting ADC Zocilurtatug Pelitecan (Zoci) for the Treatment of Neuroendocrine Carcinomas (NECs) - businesswire.combusinesswire.com · Mon, 03 Aug 2026 11:00:00 GMTInhibikase Wins FDA Orphan Status for PAH Drug Candidate - MyChesCoMyChesCo · Fri, 31 Jul 2026 21:00:00 GMTSumitomo Pharma America Announces Enzomenib (DSP-5336) Receives FDA Orphan Drug Designation for Treatment of Acute Lymphoblastic Leukemia - Yahoo FinanceYahoo Finance · Thu, 30 Jul 2026 07:00:00 GMTCellares and Papillon Therapeutics partner to scale orphan drug production - BioProcess InternationalBioProcess International · Tue, 28 Jul 2026 07:00:00 GMT