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Congressional Panel Says the United States Is Losing Its Lead on Rare Disease Cures - Medical DailyMedical Daily · Sat, 08 Aug 2026 03:30:41 GMTStudy identifies promising therapy to prevent relapses in rare neurological disease - Medical XpressMedical Xpress · Fri, 07 Aug 2026 12:00:03 GMTCAMP4 advances rare disease treatment for SYNGAP1 into human trials - CNBCCNBC · Thu, 06 Aug 2026 18:52:12 GMTNo fixes yet for costly rare disease drug program, one year after David Eby called for changes - Vancouver SunVancouver Sun · Thu, 06 Aug 2026 13:09:35 GMTCHOP, Penn-founded lab win federal millions for rare disease gene therapy - Northeast TimesNortheast Times · Thu, 06 Aug 2026 03:00:00 GMTPharmalittle: We're reading about a Medicare pilot and orphan drugs, Pfizer cutbacks, and more - STATSTAT · Wed, 05 Aug 2026 19:28:37 GMT2 Philadelphia labs receive millions in federal funding to create treatments for rare genetic diseases in 5 years - WHYYWHYY · Wed, 05 Aug 2026 09:03:56 GMTExemption of rare disease therapies in drug-pricing pilots would wipe out huge savings, analysis finds - STATSTAT · Wed, 05 Aug 2026 08:33:42 GMT